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Low-intensity ultrasound ameliorates brain organoid integration and rescues microcephaly deficits

Xiao-Hong Li, Di Guo, Li-Qun Chen, Zhe-Han Chang, Jian-Xin Shi, Nan Hu, Chong Chen, Xiao-Wang Zhang, Shuang-Qing Bao, Meng-Meng Chen, Dong Ming

Brain 2024, 147, 3817-3833 · 10.1093/brain/awae150

in vitro cellrodenthealthyothercellular imaginginvasive electrophysiologyhistology molecularbehaviour

Abstract

Human brain organoids represent a remarkable platform for modelling neurological disorders and a promising brain repair approach. However, the effects of physical stimulation on their development and integration remain unclear. Here, we report that low-intensity ultrasound significantly increases neural progenitor cell proliferation and neuronal maturation in cortical organoids. Histological assays and single-cell gene expression analyses revealed that low-intensity ultrasound improves the neural development in cortical organoids. Following organoid grafts transplantation into the injured somatosensory cortices of adult mice, longitudinal electrophysiological recordings and histological assays revealed that ultrasound-treated organoid grafts undergo advanced maturation. They also exhibit enhanced pain-related gamma-band activity and more disseminated projections into the host brain than the untreated groups. Finally, low-intensity ultrasound ameliorates neuropathological deficits in a microcephaly brain organoid model. Hence, low-intensity ultrasound stimulation advances the development and integration of brain organoids, providing a strategy for treating neurodevelopmental disorders and repairing cortical damage.

Abstract via europepmc.

Specieshuman (hPSC-derived cortical organoids); mouse (NOD/SCID)
Subjects15, 15swept preparations
Sessions per subjectnot reported
Randomisedyes
Blindingnot reported
Sham / controlno treatment control
Auditory controlnot reported
Readout timingoffline
Anaesthesianot reported
Readoutscellular imaging, invasive electrophysiology, histology molecular, behaviourImmunostaining/confocal imaging of proliferation, differentiation and synaptic markers; bulk and single-cell RNA-seq; extracellular multi-electrode recordings from organoids and host cortex; von Frey mechanical nociception behavioural test
Direction of effectmixed or unclearLIUS increased neural progenitor proliferation and reduced apoptosis, delayed early neuronal differentiation but increased later cortical-plate thickness and synapse density, enhanced organoid-graft vascularisation, synaptic integration, projection density and electrophysiological maturation after transplantation, and rescued proliferation/neurogenesis deficits in ASPM-mutant (microcephaly) organoids.
Adverse eventsnot reported

Exposures

Exposure 1: In vitro LIUS stimulation of cortical organoids

Target: brain organoid — “cortical organoid (in vitro)
Device: Mettler · Mettler Electronics · ME740

Pulse timing
Waveformnot reported
Fundamental frequency (kHz)3,000✓✓
Pulse duration (ms)not reported
Pulse repetition frequency (Hz)not reported
Duty cycle (%)not reported
Sonication duration (s)not reported
Pressure and intensity, by domain
Free-field pressure (kPa)not reported
Free-field Isppa (W/cm²)not reported
Free-field Ispta (W/cm²)not reported
In-situ estimatenot applicable
In-situ pressure (kPa)not applicable
In-situ Isppa (W/cm²)not applicable
In-situ Ispta (W/cm²)not applicable
Protocol, in the paper’s words

Cortical organoids were exposed to ultrasound starting Day 18. A range of pulse intensities (0-0.5 W) was tested with a 3 MHz plane transducer (5 cm^2 effective radiating area); the lowest intensity tested, 0.2 W, produced a significant effect and was used for all subsequent stimulation.

Exposure 2: In vivo focused LIUS stimulation of transplanted organoid grafts

Target: brain organoid, primary somatosensory cortex — “organoid graft transplanted into primary somatosensory cortex (S1)
Device: Olympus / Panametrics · Olympus · A303S-SU

Pulse timing
Waveformnot reported
Fundamental frequency (kHz)1,000✓✓
Pulse duration (ms)not reported
Pulse repetition frequency (Hz)not reported
Duty cycle (%)not reported
Sonication duration (s)not reported
Pressure and intensity, by domain
Free-field pressure (kPa)not reported
Free-field Isppa (W/cm²)not reported
Free-field Ispta (W/cm²)not reported
In-situ estimatenot reported
In-situ pressure (kPa)not reported
In-situ Isppa (W/cm²)not reported
In-situ Ispta (W/cm²)not reported
Protocol, in the paper’s words

Focused LIUS stimulation was applied to organoid grafts transplanted into the primary somatosensory cortex, for one month starting 7 days post-transplantation (in vivo LIUS stimulation group); a separate LIUS-pretreatment group had organoids stimulated in vitro before transplantation.

Flags from extraction

  • n_subjectsStudy mixes cultured organoids (subject_unit=preparation, count not totalled in main text) with living mice receiving in vivo LIUS (in vivo LIUS stimulation groups: n=15 wild-type-graft cohort, n=15 ASPM-/- cohort); no single total is stated.
  • n_sessions_per_subjectIn vitro organoids were stimulated repeatedly from Day 18 onward and in vivo grafts for one month starting 7 days post-transplantation, but the main text does not state a session count.
  • exposures[0].timingPulse duration, PRF, duty cycle, sonication duration and waveform for the in vitro/in vivo LIUS protocols are described only in a figure schematic (Fig. 1C) and in supplementary methods not present in the extracted text; not stated in the main text.
  • exposures[1].timingSame as exposures[0].timing: numeric timing parameters for in vivo organoid-graft stimulation are not given in the main text.
  • sham_typeControl organoids/mice received no ultrasound and no described sham procedure (no inactive transducer or sham device mentioned).